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What type of drug is Patisiran and how it works? select all the correct answers.
Patisiran prevents the pathological accumulation of a misfolded protein and slows down disease progression
Patisiran is a miRNA-based drug
Patisiran is used to treat a rare autosomal recessive disorder, mucopolysaccharidosis
Patisiran targets the TTR (transthyretin) mRNA
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